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Meet the P.I.

Stephanie Cherqui.jpg Dr. Cherqui received her Ph.D in 2002 at Necker hospital (Paris, France); her research project focused on the molecular characterization of cystinosis, a metabolic hereditary disease, and the generation of the mouse model.

She then specialized in stem cells and gene therapy during her post-doctoral internship at The Scripps Research Institute where she was appointed Assistant Professor in 2009.

In 2012, Dr. Cherqui joined the University of California, San Diego, Department of Pediatrics, Division of Genetics and became Associate Professor in 2016. Her lab focuses on the use of stem cell and gene therapy for multi-systemic genetic disorders and fundamental understanding of tissue repair by bone marrow stem cells. Dr. Cherqui is currently developing the first stem cell gene therapy clinical trial for cystinosis at UC San Diego.

Dr. Cherqui is the chair of the American Society of Gene and Cell Therapy (ASCGT) Gene and Cell Therapy of Genetic and Metabolic Diseases committee. She is also a member of the Scientific Review Board of the Cystinosis Research Foundation and a Scientific Council member for the Cure Cystinosis International Registry (CCIR).

Her research is funded by grants from the National Institute of Health (NIH), California Institute of Regenerative Medicine (CIRM), and the Cystinosis Research Foundation.